Protein‐Like Polymers Targeting Keap1/Nrf2 as Therapeutics for Myocardial Infarction

J Joshua M. Mesfin K Kendal P. Carrow (Medical Scientist Training Program Department of Biomedical Engineering Northwestern University Feinberg School of Medicine Chicago IL 60611 USA) A Alexander Chen M Madeline P. Hopps (Department of Chemistry International Institute for Nanotechnology Simpson‐Querrey Institute Chemistry of Life Processes Institute Northwestern University Evanston IL 60208 USA) J JoJo J. Holm (Department of Chemistry International Institute for Nanotechnology Simpson‐Querrey Institute Chemistry of Life Processes Institute Northwestern University Evanston IL 60208 USA) Q Quincy P. Lyons (Shu Chien‐Gene Lay Department of Bioengineering Sanford Consortium for Regenerative Medicine University of California San Diego La Jolla CA 92037 USA) M Michael B. Nguyen J Jervaughn D. Hunter A Assa Magassa (Department of Chemistry Department of Materials Science & Engineering Department of Pharmacology International Institute for Nanotechnology Simpson‐Querrey Institute Chemistry of Life Processes Institute Northwestern University Evanston IL 60208 USA) E Elyse G. Wong K Kate Reimold (Shu Chien‐Gene Lay Department of Bioengineering Sanford Consortium for Regenerative Medicine University of California San Diego La Jolla CA 92037 USA) S Sriya N. Paleti (Shu Chien‐Gene Lay Department of Bioengineering Sanford Consortium for Regenerative Medicine University of California San Diego La Jolla CA 92037 USA) E Emily Gardner (Shu Chien‐Gene Lay Department of Bioengineering Sanford Consortium for Regenerative Medicine University of California San Diego La Jolla CA 92037 USA) M Matthew P. Thompson (Pyrologix, Vibrant Planet) C Colin G. Luo X Xiaoyu Zhang K Karen L. Christman N Nathan C. Gianneschi (Department of Materials Science & Engineering)

Abstract

Abstract Myocardial infarction (MI) results in oxidative stress to the myocardium and frequently leads to heart failure (HF). There is an unmet clinical need to develop therapeutics that address the inflammatory stress response and prevent negative left ventricular remodeling. Here, the Keap1/Nrf2 protein–protein interaction is specifically targeted, as Nrf2 activation is known to mitigate the inflammatory response following MI. This is achieved using a Nrf2‐mimetic protein‐like polymer (PLP) to inhibit the Keap1‐Nrf2 interaction. The PLP platform technology provides stability in vivo, potent intracellular bioactivity, and multivalency leading to high avidity Keap1 binding. In vitro and in vivo assays to probe cellular activity and MI therapeutic utility are employed. These Keap1‐inhibiting PLPs (Keap1i‐PLPs) impart cytoprotection from oxidative stress via Nrf2 activation at sub‐nanomolar concentrations in primary cardiomyocytes. Single‐digit mg kg −1 , single‐dose, intravenous PLP administration significantly improves cardiac function in rats post‐MI through immunomodulatory, anti‐apoptotic, and angiogenic mechanisms. Thus Keap1i‐PLPs disrupt key intracellular protein–protein interactions following intravenous, systemic administration in vivo. These results have broad implications not only for MI but also for other oxidative stress‐driven diseases and conditions.

Article Details

Volume / Issue Vol. 37, Issue 27
Published July 01, 2025
ISSN 0935-9648
Publisher Unknown Publisher

Journal Info

Advanced Materials

Unknown Publisher

ISSN: 0935-9648 Physical Sciences

Authors (18)

J

Joshua M. Mesfin

K

Kendal P. Carrow

Medical Scientist Training Program Department of Biomedical Engineering Northwestern University Feinberg School of Medicine Chicago IL 60611 USA

A

Alexander Chen

M

Madeline P. Hopps

Department of Chemistry International Institute for Nanotechnology Simpson‐Querrey Institute Chemistry of Life Processes Institute Northwestern University Evanston IL 60208 USA

J

JoJo J. Holm

Department of Chemistry International Institute for Nanotechnology Simpson‐Querrey Institute Chemistry of Life Processes Institute Northwestern University Evanston IL 60208 USA

Q

Quincy P. Lyons

Shu Chien‐Gene Lay Department of Bioengineering Sanford Consortium for Regenerative Medicine University of California San Diego La Jolla CA 92037 USA

M

Michael B. Nguyen

J

Jervaughn D. Hunter

A

Assa Magassa

Department of Chemistry Department of Materials Science & Engineering Department of Pharmacology International Institute for Nanotechnology Simpson‐Querrey Institute Chemistry of Life Processes Institute Northwestern University Evanston IL 60208 USA

E

Elyse G. Wong

K

Kate Reimold

Shu Chien‐Gene Lay Department of Bioengineering Sanford Consortium for Regenerative Medicine University of California San Diego La Jolla CA 92037 USA

S

Sriya N. Paleti

Shu Chien‐Gene Lay Department of Bioengineering Sanford Consortium for Regenerative Medicine University of California San Diego La Jolla CA 92037 USA

E

Emily Gardner

Shu Chien‐Gene Lay Department of Bioengineering Sanford Consortium for Regenerative Medicine University of California San Diego La Jolla CA 92037 USA

M

Matthew P. Thompson

Pyrologix, Vibrant Planet

C

Colin G. Luo

X

Xiaoyu Zhang

K

Karen L. Christman

N

Nathan C. Gianneschi

Department of Materials Science & Engineering