Tumor-Intrinsic and Microenvironmental Determinants of Impaired Antitumor Immunity in Chromophobe Renal Cell Carcinoma

C Chris Labaki (Beth Israel Deaconess Medical Center, Boston, MA) E Eddy Saad K Katrine N. Madsen (Center of Molecular and Cellular Oncology (CMCO), Yale School of Medicine, New Haven, CT) C Charbel Hobeika (Department of Medicine, Cleveland Clinic Fairview Hospital, Cleveland, OH) K Kevin Bi M Michel Alchoueiry (Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA) S Sabrina Camp Y Yue Hou (Department of Mechanical Engineering) Z Ziad Bakouny (Memorial Sloan Kettering Cancer Center) S Sayed Matar N Nourhan El Ahmar J Jackson Nyman (PathAI, Inc, Boston, MA) L Long Zhang C Carmen Priolo (Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA) R Rishabh Rout (Center of Molecular and Cellular Oncology, Yale Cancer Center, Yale School of Medicine, New Haven, CT) M Melissa Daou (Department of Medicine, Yale University, New Haven, CT) D Damir Khabibullin (Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA) S Samer Salem (Cleveland Clinic, Cleveland, OH) N Nicholas Schindler (Center of Molecular and Cellular Oncology (CMCO), Yale School of Medicine, New Haven, CT) R Renee Maria Saliby (Center of Molecular and Cellular Oncology, Yale Cancer Center, Yale School of Medicine, New Haven, CT) K Kevin Meli J J. Connor Wells (Arthur JE Child Comprehensive Cancer Centre, Calgary, AB, Canada) E Erica Pimenta K Kosuke Takemura (Faculty of Economics, Shiga University) J Jihye Park (Department of Chemistry) M Marc Eid (Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA) K Karl Semaan (Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA) J Jingxin Fu (Department of Chemistry, University of California, One Shields Avenue, Davis, California 95616, United States) T Thomas Denize (Department of Pathology, Massachusetts General Hospital, Boston) R Razane El Hajj Chehade (Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA) M Marc Machaalani R Rashad Nawfal (Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA) W Wassim Daoud Khatoun (Dana-Farber Cancer Institute, Boston, MA) M Mustafa Saleh J Jad El Masri N Nina Rossa Haddad W Wenxin Xu (Department of Medical Oncology Dana‐Farber Cancer Institute Boston Massachusetts USA) B Bradley A. McGregor M Michelle S. Hirsch W Wanling Xie (Department of Medical Oncology Dana‐Farber Cancer Institute Boston Massachusetts USA) D Daniel Y.C. Heng (Tom Baker Cancer Centre, University of Calgary, Calgary, AB, Canada) D David F. McDermott (Division of Medical Oncology, Department of Medicine Beth Israel Deaconess Medical Center Boston Massachusetts USA) S Sabina Signoretti E Eliezer M. Van Allen S Sachet A. Shukla T Toni K. Choueiri (Department of Medical Oncology Dana‐Farber Cancer Institute Boston Massachusetts USA) E Elizabeth P. Henske (Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA) D David A. Braun

Abstract

PURPOSE While immune checkpoint inhibition (ICI) has transformed the management of many advanced renal cell carcinomas (RCCs), the determinants of effective antitumor immunity for chromophobe RCC (ChRCC) and renal oncocytic tumors remain an unmet clinical and scientific need. METHODS Single-cell transcriptomic and T-cell receptor profiling was performed on tumor and adjacent normal tissue of patients with ChRCC and renal oncocytic neoplasms. Using machine learning, the cellular origin of renal oncocytic neoplasms was evaluated, with analysis of associated oncogenic pathways. Using immunohistochemistry, immune infiltration was analyzed in renal oncocytic neoplasms in comparison with clear cell RCC (ccRCC). Immune checkpoint expression, clonal expansion, and tumor specificity were compared between ChRCC and ccRCC. Using the International Metastatic RCC Database Consortium data set, clinical outcomes of patients with metastatic ChRCC (mChRCC) treated with first-line systemic regimens were compared with those of patients with ccRCC. RESULTS We validated α-intercalated cells as the cellular origin of renal oncocytic neoplasms. We identified a downregulation of HLA class I molecules with enrichment of potentially targetable pathways including mammalian target of rapamycin and ferroptosis in ChRCC. The tumor microenvironment of ChRCC showed markedly decreased immune infiltration, with a pronounced depletion in tumor-infiltrating CD8 + T cells. ChRCC-infiltrating CD8 + T cells demonstrated lower immune checkpoint expression, diminished clonal expansion, and decreased tumor specificity. Clinical analysis identified poor survival outcomes selectively among patients with mChRCC treated with immune-based therapies. CONCLUSION Immunogenomic analysis of ChRCC revealed profound depletion of T cells, with an immune phenotype marked by a lack of expression of immune checkpoints and poor tumor specificity, suggesting that the few T cells in these tumor types are likely nonspecific bystanders. This immune-cold environment hinders an effective response to immunotherapy and underscores the need for ChRCC-tailored treatments designed to improve tumor-specific T-cell infiltration into the microenvironment.

Article Details

Volume / Issue Vol. 43, Issue 23
Published August 10, 2025
Pages 2639-2654
ISSN 0732-183X
Publisher Lippincott Williams & Wilkins

Journal Info

Journal of Clinical Oncology

Lippincott Williams & Wilkins

ISSN: 0732-183X Health Sciences

Authors (48)

C

Chris Labaki

Beth Israel Deaconess Medical Center, Boston, MA

E

Eddy Saad

K

Katrine N. Madsen

Center of Molecular and Cellular Oncology (CMCO), Yale School of Medicine, New Haven, CT

C

Charbel Hobeika

Department of Medicine, Cleveland Clinic Fairview Hospital, Cleveland, OH

K

Kevin Bi

M

Michel Alchoueiry

Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA

S

Sabrina Camp

Y

Yue Hou

Department of Mechanical Engineering

Z

Ziad Bakouny

Memorial Sloan Kettering Cancer Center

S

Sayed Matar

N

Nourhan El Ahmar

J

Jackson Nyman

PathAI, Inc, Boston, MA

L

Long Zhang

C

Carmen Priolo

Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA

R

Rishabh Rout

Center of Molecular and Cellular Oncology, Yale Cancer Center, Yale School of Medicine, New Haven, CT

M

Melissa Daou

Department of Medicine, Yale University, New Haven, CT

D

Damir Khabibullin

Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA

S

Samer Salem

Cleveland Clinic, Cleveland, OH

N

Nicholas Schindler

Center of Molecular and Cellular Oncology (CMCO), Yale School of Medicine, New Haven, CT

R

Renee Maria Saliby

Center of Molecular and Cellular Oncology, Yale Cancer Center, Yale School of Medicine, New Haven, CT

K

Kevin Meli

J

J. Connor Wells

Arthur JE Child Comprehensive Cancer Centre, Calgary, AB, Canada

E

Erica Pimenta

K

Kosuke Takemura

Faculty of Economics, Shiga University

J

Jihye Park

Department of Chemistry

M

Marc Eid

Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA

K

Karl Semaan

Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA

J

Jingxin Fu

Department of Chemistry, University of California, One Shields Avenue, Davis, California 95616, United States

T

Thomas Denize

Department of Pathology, Massachusetts General Hospital, Boston

R

Razane El Hajj Chehade

Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA

M

Marc Machaalani

R

Rashad Nawfal

Dana-Farber Cancer Institute, Harvard Medical School, Boston, MA

W

Wassim Daoud Khatoun

Dana-Farber Cancer Institute, Boston, MA

M

Mustafa Saleh

J

Jad El Masri

N

Nina Rossa Haddad

W

Wenxin Xu

Department of Medical Oncology Dana‐Farber Cancer Institute Boston Massachusetts USA

B

Bradley A. McGregor

M

Michelle S. Hirsch

W

Wanling Xie

Department of Medical Oncology Dana‐Farber Cancer Institute Boston Massachusetts USA

D

Daniel Y.C. Heng

Tom Baker Cancer Centre, University of Calgary, Calgary, AB, Canada

D

David F. McDermott

Division of Medical Oncology, Department of Medicine Beth Israel Deaconess Medical Center Boston Massachusetts USA

S

Sabina Signoretti

E

Eliezer M. Van Allen

S

Sachet A. Shukla

T

Toni K. Choueiri

Department of Medical Oncology Dana‐Farber Cancer Institute Boston Massachusetts USA

E

Elizabeth P. Henske

Pulmonary and Critical Care Medicine, Department of Medicine, Brigham and Women's Hospital, Harvard Medical School, Boston, MA

D

David A. Braun